Concepts in Gene Therapy / / ed. by John A. Barranger, Michael Strauss.

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Superior document:Title is part of eBook package: De Gruyter DGBA Physical Sciences 1990 - 1999
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Place / Publishing House:Berlin ;, Boston : : De Gruyter, , [2020]
©1997
Year of Publication:2020
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Language:English
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spelling Concepts in Gene Therapy / ed. by John A. Barranger, Michael Strauss.
Reprint 2020
Berlin ; Boston : De Gruyter, [2020]
©1997
1 online resource (553 p.)
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Frontmatter -- Preface -- Contents -- I. Methods of Gene Delivery -- 1. Retroviral Vectors -- 2. Adenoviral Vectors -- 3. Herpes Simplex Virus Mediated Gene Transfer to Neurons -- 4. Adeno-Associated Viral Vectors -- 5. Virus Functions for Artificial Vectors -- 6. Targeted Gene Delivery and Expression in Hepatocytes -- 7. Particle-Mediated Gene Delivery System for Cancer Research -- II. Methods for Inactivation or Restoration of Gene Function -- 8. Gene Inactivation by Homologous Recombination - Animal Models of Plasma Lipoprotein Disorders -- 9. Potential Antisense Oligonucleotide Therapies for Neurodegenerative Diseases -- 10. Synthetic Ribozymes: The Hammerhead Ribozyme -- 11. Ribozymes as Tools for the Gene Therapist -- III. Cellular Target Systems -- 12. Gene Transfer and Transgene Expression in Hematopoietic Cells -- 13. The Liver as a Target for Gene Therapy -- 14. Gene Therapy for Gaucher Disease via Genetically Engineered Primary Myoblasts -- 15. In vivo Secretion of Therapeutic Proteins from Neo-Organs -- IV. Genetic Diseases -- 16. Gene Therapy for Cystic Fibrosis - Strategies, Problems and Perspectives -- 17. Gene Therapy for Dystrophin Deficiency -- 18. Gene Therapy For Familial Hypercholesterolemia -- 19. Therapeutic Strategies for the Lysosomal Storage Disorders -- V. Non-Genetic and Infectious Diseases -- 20. Gene Therapy for Arthritis -- 21. Gene Therapy for HIV-1 Disease -- VI. Cancer -- 22. Suicide Genes for the Treatment of Cancer -- 23. Tumor Cell Vaccines Using Genetically Modified Cells Coexpressing Cytokines and the T Cell Costimulatory Molecule B7 -- 24. Dosage Impact on Immunotherapy with Cytokine-Gene Modified Cancer Vaccines -- 25. Tumor Suppressor Gene Therapy - Growth Arrest and Programmed Cell Death -- Acknowledgement -- References -- Contributors -- Index
restricted access http://purl.org/coar/access_right/c_16ec online access with authorization star
Mode of access: Internet via World Wide Web.
In English.
Description based on online resource; title from PDF title page (publisher's Web site, viewed 30. Aug 2021)
Gentherapie.
SCIENCE / Life Sciences / Biology. bisacsh
Bahnson, Alfred, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Ball, Edward, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Barranger, John A., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Barranger, John A., editor. edt http://id.loc.gov/vocabulary/relators/edt
Baum, Christopher, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Beeler, Margeret, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Blankenstein, Thomas, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Bohl, Delphine, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Bohnlein, Ernst, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Brand, Karsten, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Cayeux, Sophie, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Cichon, Gunter, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Coutelle, Charles, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Culver, Kenneth W., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Dedieu, Jean-François, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Dickson, George, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Dorken, Bernd, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Dunigan, James, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Eckert, Hans-Georg, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Eckstein, Fritz, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Evans, Christopher H., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Fink, D. J., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Ghivizzani, Steven C., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Ginzberg, Dalia, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Glorioso, J. C., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Goins, W. F., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Gotthardt, Michael, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Grifman, Mirta, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Gunzburg, Walter H., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Heard, Michel, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Heidenreich, Olaf, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Herz, Joachim, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Kang, Richard, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Kemp, Amy, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Krisky, D., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Lancia, Jason, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Learish, Randall, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Lev-Lehman, Efrat, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Liu, Chunming, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Mannion-Henderson, Jane, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Marconi, P., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
McCarty, D. M., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Mierski, Joseph, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Milich, Lynn, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Mohney, Trina, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Nimgaonkar, Maya, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Oligino, T., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Orsini, Cécile, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Ostertag, Wolfram, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Perricaudet, Michel, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Poliani, P. L., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Rakhmilevich, Alexander L., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Ramakrishnan, R., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Rice, Erin, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Robbins, Paul D., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Salmons, Brian, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Samulski, R. J., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Sandig, Volker, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Schmidt, Walter, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Schuster, Herbert, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Soreq, Hermona, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Stocking, Carol, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Strauss, Michael, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Strauss, Michael, editor. edt http://id.loc.gov/vocabulary/relators/edt
Sullenger, Bruce A., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Vallor, Michael J., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Vigne, Emmanuelle, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Wagener, Thomas, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Watkins, Simon, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Willnow, Thomas E., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Wu, Catherine H., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Wu, George Y., contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Yang, Ning-Sun, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Yeh, Patrice, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Zakut, Haim, contributor. ctb https://id.loc.gov/vocabulary/relators/ctb
Title is part of eBook package: De Gruyter DGBA Physical Sciences 1990 - 1999 9783110637236 ZDB-23-GPS
print 9783110149845
https://doi.org/10.1515/9783110808636
https://www.degruyter.com/isbn/9783110808636
Cover https://www.degruyter.com/cover/covers/9783110808636.jpg
language English
format eBook
author2 Bahnson, Alfred,
Bahnson, Alfred,
Ball, Edward,
Ball, Edward,
Barranger, John A.,
Barranger, John A.,
Barranger, John A.,
Barranger, John A.,
Baum, Christopher,
Baum, Christopher,
Beeler, Margeret,
Beeler, Margeret,
Blankenstein, Thomas,
Blankenstein, Thomas,
Bohl, Delphine,
Bohl, Delphine,
Bohnlein, Ernst,
Bohnlein, Ernst,
Brand, Karsten,
Brand, Karsten,
Cayeux, Sophie,
Cayeux, Sophie,
Cichon, Gunter,
Cichon, Gunter,
Coutelle, Charles,
Coutelle, Charles,
Culver, Kenneth W.,
Culver, Kenneth W.,
Dedieu, Jean-François,
Dedieu, Jean-François,
Dickson, George,
Dickson, George,
Dorken, Bernd,
Dorken, Bernd,
Dunigan, James,
Dunigan, James,
Eckert, Hans-Georg,
Eckert, Hans-Georg,
Eckstein, Fritz,
Eckstein, Fritz,
Evans, Christopher H.,
Evans, Christopher H.,
Fink, D. J.,
Fink, D. J.,
Ghivizzani, Steven C.,
Ghivizzani, Steven C.,
Ginzberg, Dalia,
Ginzberg, Dalia,
Glorioso, J. C.,
Glorioso, J. C.,
Goins, W. F.,
Goins, W. F.,
Gotthardt, Michael,
Gotthardt, Michael,
Grifman, Mirta,
Grifman, Mirta,
Gunzburg, Walter H.,
Gunzburg, Walter H.,
Heard, Michel,
Heard, Michel,
Heidenreich, Olaf,
Heidenreich, Olaf,
Herz, Joachim,
Herz, Joachim,
Kang, Richard,
Kang, Richard,
Kemp, Amy,
Kemp, Amy,
Krisky, D.,
Krisky, D.,
Lancia, Jason,
Lancia, Jason,
Learish, Randall,
Learish, Randall,
Lev-Lehman, Efrat,
Lev-Lehman, Efrat,
Liu, Chunming,
Liu, Chunming,
Mannion-Henderson, Jane,
Mannion-Henderson, Jane,
Marconi, P.,
Marconi, P.,
McCarty, D. M.,
McCarty, D. M.,
Mierski, Joseph,
Mierski, Joseph,
Milich, Lynn,
Milich, Lynn,
Mohney, Trina,
Mohney, Trina,
Nimgaonkar, Maya,
Nimgaonkar, Maya,
Oligino, T.,
Oligino, T.,
Orsini, Cécile,
Orsini, Cécile,
Ostertag, Wolfram,
Ostertag, Wolfram,
Perricaudet, Michel,
Perricaudet, Michel,
Poliani, P. L.,
Poliani, P. L.,
Rakhmilevich, Alexander L.,
Rakhmilevich, Alexander L.,
Ramakrishnan, R.,
Ramakrishnan, R.,
Rice, Erin,
Rice, Erin,
Robbins, Paul D.,
Robbins, Paul D.,
Salmons, Brian,
Salmons, Brian,
Samulski, R. J.,
Samulski, R. J.,
Sandig, Volker,
Sandig, Volker,
Schmidt, Walter,
Schmidt, Walter,
Schuster, Herbert,
Schuster, Herbert,
Soreq, Hermona,
Soreq, Hermona,
Stocking, Carol,
Stocking, Carol,
Strauss, Michael,
Strauss, Michael,
Strauss, Michael,
Strauss, Michael,
Sullenger, Bruce A.,
Sullenger, Bruce A.,
Vallor, Michael J.,
Vallor, Michael J.,
Vigne, Emmanuelle,
Vigne, Emmanuelle,
Wagener, Thomas,
Wagener, Thomas,
Watkins, Simon,
Watkins, Simon,
Willnow, Thomas E.,
Willnow, Thomas E.,
Wu, Catherine H.,
Wu, Catherine H.,
Wu, George Y.,
Wu, George Y.,
Yang, Ning-Sun,
Yang, Ning-Sun,
Yeh, Patrice,
Yeh, Patrice,
Zakut, Haim,
Zakut, Haim,
author_facet Bahnson, Alfred,
Bahnson, Alfred,
Ball, Edward,
Ball, Edward,
Barranger, John A.,
Barranger, John A.,
Barranger, John A.,
Barranger, John A.,
Baum, Christopher,
Baum, Christopher,
Beeler, Margeret,
Beeler, Margeret,
Blankenstein, Thomas,
Blankenstein, Thomas,
Bohl, Delphine,
Bohl, Delphine,
Bohnlein, Ernst,
Bohnlein, Ernst,
Brand, Karsten,
Brand, Karsten,
Cayeux, Sophie,
Cayeux, Sophie,
Cichon, Gunter,
Cichon, Gunter,
Coutelle, Charles,
Coutelle, Charles,
Culver, Kenneth W.,
Culver, Kenneth W.,
Dedieu, Jean-François,
Dedieu, Jean-François,
Dickson, George,
Dickson, George,
Dorken, Bernd,
Dorken, Bernd,
Dunigan, James,
Dunigan, James,
Eckert, Hans-Georg,
Eckert, Hans-Georg,
Eckstein, Fritz,
Eckstein, Fritz,
Evans, Christopher H.,
Evans, Christopher H.,
Fink, D. J.,
Fink, D. J.,
Ghivizzani, Steven C.,
Ghivizzani, Steven C.,
Ginzberg, Dalia,
Ginzberg, Dalia,
Glorioso, J. C.,
Glorioso, J. C.,
Goins, W. F.,
Goins, W. F.,
Gotthardt, Michael,
Gotthardt, Michael,
Grifman, Mirta,
Grifman, Mirta,
Gunzburg, Walter H.,
Gunzburg, Walter H.,
Heard, Michel,
Heard, Michel,
Heidenreich, Olaf,
Heidenreich, Olaf,
Herz, Joachim,
Herz, Joachim,
Kang, Richard,
Kang, Richard,
Kemp, Amy,
Kemp, Amy,
Krisky, D.,
Krisky, D.,
Lancia, Jason,
Lancia, Jason,
Learish, Randall,
Learish, Randall,
Lev-Lehman, Efrat,
Lev-Lehman, Efrat,
Liu, Chunming,
Liu, Chunming,
Mannion-Henderson, Jane,
Mannion-Henderson, Jane,
Marconi, P.,
Marconi, P.,
McCarty, D. M.,
McCarty, D. M.,
Mierski, Joseph,
Mierski, Joseph,
Milich, Lynn,
Milich, Lynn,
Mohney, Trina,
Mohney, Trina,
Nimgaonkar, Maya,
Nimgaonkar, Maya,
Oligino, T.,
Oligino, T.,
Orsini, Cécile,
Orsini, Cécile,
Ostertag, Wolfram,
Ostertag, Wolfram,
Perricaudet, Michel,
Perricaudet, Michel,
Poliani, P. L.,
Poliani, P. L.,
Rakhmilevich, Alexander L.,
Rakhmilevich, Alexander L.,
Ramakrishnan, R.,
Ramakrishnan, R.,
Rice, Erin,
Rice, Erin,
Robbins, Paul D.,
Robbins, Paul D.,
Salmons, Brian,
Salmons, Brian,
Samulski, R. J.,
Samulski, R. J.,
Sandig, Volker,
Sandig, Volker,
Schmidt, Walter,
Schmidt, Walter,
Schuster, Herbert,
Schuster, Herbert,
Soreq, Hermona,
Soreq, Hermona,
Stocking, Carol,
Stocking, Carol,
Strauss, Michael,
Strauss, Michael,
Strauss, Michael,
Strauss, Michael,
Sullenger, Bruce A.,
Sullenger, Bruce A.,
Vallor, Michael J.,
Vallor, Michael J.,
Vigne, Emmanuelle,
Vigne, Emmanuelle,
Wagener, Thomas,
Wagener, Thomas,
Watkins, Simon,
Watkins, Simon,
Willnow, Thomas E.,
Willnow, Thomas E.,
Wu, Catherine H.,
Wu, Catherine H.,
Wu, George Y.,
Wu, George Y.,
Yang, Ning-Sun,
Yang, Ning-Sun,
Yeh, Patrice,
Yeh, Patrice,
Zakut, Haim,
Zakut, Haim,
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author_sort Bahnson, Alfred,
title Concepts in Gene Therapy /
spellingShingle Concepts in Gene Therapy /
Frontmatter --
Preface --
Contents --
I. Methods of Gene Delivery --
1. Retroviral Vectors --
2. Adenoviral Vectors --
3. Herpes Simplex Virus Mediated Gene Transfer to Neurons --
4. Adeno-Associated Viral Vectors --
5. Virus Functions for Artificial Vectors --
6. Targeted Gene Delivery and Expression in Hepatocytes --
7. Particle-Mediated Gene Delivery System for Cancer Research --
II. Methods for Inactivation or Restoration of Gene Function --
8. Gene Inactivation by Homologous Recombination - Animal Models of Plasma Lipoprotein Disorders --
9. Potential Antisense Oligonucleotide Therapies for Neurodegenerative Diseases --
10. Synthetic Ribozymes: The Hammerhead Ribozyme --
11. Ribozymes as Tools for the Gene Therapist --
III. Cellular Target Systems --
12. Gene Transfer and Transgene Expression in Hematopoietic Cells --
13. The Liver as a Target for Gene Therapy --
14. Gene Therapy for Gaucher Disease via Genetically Engineered Primary Myoblasts --
15. In vivo Secretion of Therapeutic Proteins from Neo-Organs --
IV. Genetic Diseases --
16. Gene Therapy for Cystic Fibrosis - Strategies, Problems and Perspectives --
17. Gene Therapy for Dystrophin Deficiency --
18. Gene Therapy For Familial Hypercholesterolemia --
19. Therapeutic Strategies for the Lysosomal Storage Disorders --
V. Non-Genetic and Infectious Diseases --
20. Gene Therapy for Arthritis --
21. Gene Therapy for HIV-1 Disease --
VI. Cancer --
22. Suicide Genes for the Treatment of Cancer --
23. Tumor Cell Vaccines Using Genetically Modified Cells Coexpressing Cytokines and the T Cell Costimulatory Molecule B7 --
24. Dosage Impact on Immunotherapy with Cytokine-Gene Modified Cancer Vaccines --
25. Tumor Suppressor Gene Therapy - Growth Arrest and Programmed Cell Death --
Acknowledgement --
References --
Contributors --
Index
title_full Concepts in Gene Therapy / ed. by John A. Barranger, Michael Strauss.
title_fullStr Concepts in Gene Therapy / ed. by John A. Barranger, Michael Strauss.
title_full_unstemmed Concepts in Gene Therapy / ed. by John A. Barranger, Michael Strauss.
title_auth Concepts in Gene Therapy /
title_alt Frontmatter --
Preface --
Contents --
I. Methods of Gene Delivery --
1. Retroviral Vectors --
2. Adenoviral Vectors --
3. Herpes Simplex Virus Mediated Gene Transfer to Neurons --
4. Adeno-Associated Viral Vectors --
5. Virus Functions for Artificial Vectors --
6. Targeted Gene Delivery and Expression in Hepatocytes --
7. Particle-Mediated Gene Delivery System for Cancer Research --
II. Methods for Inactivation or Restoration of Gene Function --
8. Gene Inactivation by Homologous Recombination - Animal Models of Plasma Lipoprotein Disorders --
9. Potential Antisense Oligonucleotide Therapies for Neurodegenerative Diseases --
10. Synthetic Ribozymes: The Hammerhead Ribozyme --
11. Ribozymes as Tools for the Gene Therapist --
III. Cellular Target Systems --
12. Gene Transfer and Transgene Expression in Hematopoietic Cells --
13. The Liver as a Target for Gene Therapy --
14. Gene Therapy for Gaucher Disease via Genetically Engineered Primary Myoblasts --
15. In vivo Secretion of Therapeutic Proteins from Neo-Organs --
IV. Genetic Diseases --
16. Gene Therapy for Cystic Fibrosis - Strategies, Problems and Perspectives --
17. Gene Therapy for Dystrophin Deficiency --
18. Gene Therapy For Familial Hypercholesterolemia --
19. Therapeutic Strategies for the Lysosomal Storage Disorders --
V. Non-Genetic and Infectious Diseases --
20. Gene Therapy for Arthritis --
21. Gene Therapy for HIV-1 Disease --
VI. Cancer --
22. Suicide Genes for the Treatment of Cancer --
23. Tumor Cell Vaccines Using Genetically Modified Cells Coexpressing Cytokines and the T Cell Costimulatory Molecule B7 --
24. Dosage Impact on Immunotherapy with Cytokine-Gene Modified Cancer Vaccines --
25. Tumor Suppressor Gene Therapy - Growth Arrest and Programmed Cell Death --
Acknowledgement --
References --
Contributors --
Index
title_new Concepts in Gene Therapy /
title_sort concepts in gene therapy /
publisher De Gruyter,
publishDate 2020
physical 1 online resource (553 p.)
edition Reprint 2020
contents Frontmatter --
Preface --
Contents --
I. Methods of Gene Delivery --
1. Retroviral Vectors --
2. Adenoviral Vectors --
3. Herpes Simplex Virus Mediated Gene Transfer to Neurons --
4. Adeno-Associated Viral Vectors --
5. Virus Functions for Artificial Vectors --
6. Targeted Gene Delivery and Expression in Hepatocytes --
7. Particle-Mediated Gene Delivery System for Cancer Research --
II. Methods for Inactivation or Restoration of Gene Function --
8. Gene Inactivation by Homologous Recombination - Animal Models of Plasma Lipoprotein Disorders --
9. Potential Antisense Oligonucleotide Therapies for Neurodegenerative Diseases --
10. Synthetic Ribozymes: The Hammerhead Ribozyme --
11. Ribozymes as Tools for the Gene Therapist --
III. Cellular Target Systems --
12. Gene Transfer and Transgene Expression in Hematopoietic Cells --
13. The Liver as a Target for Gene Therapy --
14. Gene Therapy for Gaucher Disease via Genetically Engineered Primary Myoblasts --
15. In vivo Secretion of Therapeutic Proteins from Neo-Organs --
IV. Genetic Diseases --
16. Gene Therapy for Cystic Fibrosis - Strategies, Problems and Perspectives --
17. Gene Therapy for Dystrophin Deficiency --
18. Gene Therapy For Familial Hypercholesterolemia --
19. Therapeutic Strategies for the Lysosomal Storage Disorders --
V. Non-Genetic and Infectious Diseases --
20. Gene Therapy for Arthritis --
21. Gene Therapy for HIV-1 Disease --
VI. Cancer --
22. Suicide Genes for the Treatment of Cancer --
23. Tumor Cell Vaccines Using Genetically Modified Cells Coexpressing Cytokines and the T Cell Costimulatory Molecule B7 --
24. Dosage Impact on Immunotherapy with Cytokine-Gene Modified Cancer Vaccines --
25. Tumor Suppressor Gene Therapy - Growth Arrest and Programmed Cell Death --
Acknowledgement --
References --
Contributors --
Index
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